Episode 6: Leveraging Real World Evidence for Advanced Therapy

This episode explores how real-world evidence is changing healthcare, its value in improving patients’ outcomes, its role in supporting R&D in advanced therapy and uptake of this innovation by health systems. It will discuss issues such as how to deal with evidence gaps in HTA and the role of RWE. It will reflect on the importance of the European Health Data Space in leveraging RWE collected in Europe and its benefits for rare disease patients. It will also look at how to ensure that health data is efficiently leveraged to help the development of advanced therapy in a sustainable, patient-centric, manner, patient engagement in data collection efforts and the role of clinicians. 

Guests: 

 Marcus Guardian (COO, EUnetHTA)

Prof. Marijke van den Berg (Director, European Paediatric Network for Haemophilia Management (PEDNET))