Antisense, gene therapy, and stem cell news, and the Blues Brothers
Dec 15, 2022•1 hr 26 min•Season 1Ep. 59
Episode description
"I want four fried chickens and a Coke". Dr. Charis Himeda joins us as we discuss some encouraging recent data from Sarepta for one of their DMD gene therapy trials and from Avidity for their myotonic dystrophy phase I/II trial and how it all potentially impacts FSHD. In addition, we revisit the potential (or lack there of) for placental or umbilical cord derived stem cell therapy for FSHD.
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