Life-Changing Gene Therapy for Beta-Thalassemia Patients with Jennifer Schneiderman, MD - podcast episode cover

Life-Changing Gene Therapy for Beta-Thalassemia Patients with Jennifer Schneiderman, MD

Apr 25, 202220 min
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Episode description

A novel gene therapy promoted transfusion independence in more than 90 percent of adult and pediatric patients with transfusion-dependent beta-thalassemia. Study co-author Jennifer Schneiderman, MD, discusses results, published in the New England Journal of Medicine.
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Life-Changing Gene Therapy for Beta-Thalassemia Patients with Jennifer Schneiderman, MD | Breakthroughs podcast - Listen or read transcript on Metacast